Sustained Correction of X-Linked Severe Combined Immunodeficiency by ex Vivo Gene Therapy

Nom de la revue
New England Journal of Medicine
Salima Hacein-Bey-Abina, Françoise Le Deist, Frédérique Carlier, Cécile Bouneaud, Christophe Hue, Jean-Pierre De Villartay, Adrian J. Thrasher, Nicolas Wulffraat, Ricardo Sorensen, Sophie Dupuis-Girod, Alain Fischer, E. Graham Davies, Wietse Kuis, Lilly Leiva, Marina Cavazzana-Calvo